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Considerations for evaluating the effectiveness and long-term outcome of enzyme replacement therapy in Pompe disease
Chong Kun Cheon
Clin Exp Pediatr. 2020;63(1):14-15.   Published online August 7, 2019
DOI: https://doi.org/10.3345/kjp.2018.07402

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Considerations for evaluating the effectiveness and long-term outcome of enzyme replacement therapy in Pompe disease
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