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Advancing orphan drug development for rare diseases
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Clin Exp Pediatr. 2024;67(7):356-357. Published online 2023 Nov 17 DOI: https://doi.org/10.3345/cep.2023.01109
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Visual Research of Global Orphan Drug from a Bibliometric Perspective
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Drug Design, Development and Therapy.2025; Volume 19: 4201. CrossRef Orphan Drug Development for Rare Diseases: Therapeutic Challenges, Translational Strategies, and Global Health Equity
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